Abstract Submission Deadline: Dec 16, 2025 - Don’t miss out – Early Bird Registration closes on Dec 18, 2025 - Submit your abstract and secure your spot today!
Rare Diseases and Orphan Drugs
Orphan Drug Development & Challenges
COVID-Driven Rare Insights
Genetic & Hematologic Rare Disorders
Rare Cancers & Drug Development
Rare Hepatic and Renal Disorders
Newborn Screening & Rare Pediatric Disorders
Rare Endocrine and Neurological Disorders
Approaches to Rare Disease Diagnosis
Novel Therapies for Rare Diseases
Drug Repurposing
Cystic Fibrosis
Cardiovascular & Respiratory Rare Disorders
Biomedical Research
AI in Rare Diseases and Orphan Drugs
Precision and Personalized Medicine
Advances in Rare Disease Research
Rare Skin Diseases
Epidemiology and Disease Control
Biomarker Importance in Rare Diseases
Orphan Drug Pricing and Market Dynamics
Functional Genomics & Gene Therapy for Rare Diseases
Public Health Perspectives in Rare Diseases
Ethical & Regulatory Challenges
Rare Diseases and Orphan Drugs
This track explores the scientific, clinical, and regulatory landscape of rare diseases and the development of orphan medicines. It highlights unmet needs, therapeutic gaps, and global efforts to improve patient access. Discussions emphasize innovation, policy frameworks, and collaboration across sectors.
Orphan Drug Development & Challenges
Focuses on the full journey of orphan drug development—from discovery to market access. Addresses challenges such as small patient populations, high research costs, regulatory hurdles, and clinical trial design limitations. The track highlights new models and methodologies that accelerate development.
COVID-Driven Rare Insights
Examines how COVID-19 accelerated rare disease research through technology, remote monitoring, and rapid clinical trial models. Highlights immunological and genomic insights gained from the pandemic. Shows how these lessons inspire new therapeutic approaches.
Genetic & Hematologic Rare Disorders
Covers advances in diagnosing and managing genetic and blood-related rare diseases. Sessions explore molecular mechanisms, genotype–phenotype correlations, and therapeutic innovations. Emphasis is placed on improving patient outcomes through early detection and precision treatment.
Rare Cancers & Drug Development
This stream addresses challenges in researching and treating rare cancers, where small patient communities limit standard clinical trials. Focus includes biomarker-driven therapies, accelerated approvals, and emerging oncology innovations. Case studies highlight successful rare cancer treatment models.
Rare Hepatic and Renal Disorders
Focuses on uncommon liver and kidney diseases, diagnostic complexities, and evolving treatment strategies. Includes updates on metabolic disorders, fibrosis, and genetic kidney conditions. Emphasizes early intervention.
Newborn Screening & Rare Pediatric Disorders
Examines the expanding role of newborn screening in early detection of rare diseases. Highlights innovations in metabolic, genetic, and endocrine testing to prevent disability and mortality. Focus includes pediatric case studies and improving long-term patient outcomes.
Rare Endocrine and Neurological Disorders
Discusses rare conditions affecting hormonal and neurological systems, including pathophysiology, diagnosis, and treatment strategies. Features updates on neurogenetics, metabolic disorders, and endocrine dysregulation. Emphasis on improving quality of life for patients with complex symptoms.
Approaches to Rare Disease Diagnosis
Showcases cutting-edge diagnostic tools, including whole-genome sequencing, metabolomics, and AI-based pattern recognition. Focuses on reducing diagnostic delays and improving accuracy. Highlights multidisciplinary diagnostic strategies.
Novel Therapies for Rare Diseases
Showcases breakthroughs such as gene editing, mRNA therapies, regenerative medicine, and targeted biologics. Sessions highlight translational research that brings novel therapies from lab to clinic. Focused on overcoming historical treatment limitations.
Drug Repurposing
Explores how existing drugs are being evaluated for new rare disease indications to reduce development time and cost. Highlights successful repurposing case studies and regulatory pathways. Emphasizes innovation through resource optimization.
Cystic Fibrosis
Dedicated to understanding CF disease progression, CFTR modulators, and emerging therapeutic technologies. Discusses challenges in lung function preservation, infection control, and personalized treatment. Highlights improved survival outcomes and long-term management.
Cardiovascular & Respiratory Rare Disorders
Addresses rare cardiac and pulmonary conditions with complex presentations. Focus includes diagnostic advancements, new drug developments, and clinical management strategies. Highlights multidisciplinary care.
Biomedical Research
Covers foundational and translational research driving progress in rare disease biology and therapy. Discusses animal models, cellular studies, and molecular pathways. Highlights how basic research fuels clinical innovation.
AI in Rare Diseases and Orphan Drugs
Discusses how AI accelerates diagnosis, drug discovery, predictive modeling, and patient stratification. Covers machine learning applications addressing small datasets. Emphasizes how digital tools improve clinical outcomes.
Precision and Personalized Medicine
Focuses on individualized clinical approaches based on genomic, proteomic, and molecular insights. Highlights personalized treatment pathways, predictive analytics, and patient-specific therapies. Bridges research and real-world care.
Advances in Rare Disease Research
Summarizes cutting-edge research across biomedical, clinical, and translational domains. Highlights breakthroughs in disease modeling, therapeutic targets, and patient care. Emphasis on accelerating innovation through collaboration.
Rare Skin Diseases
Covers dermatological rare disorders including genetic syndromes, autoimmune skin diseases, and rare inflammatory conditions. Focuses on diagnosis, clinical management, and emerging therapeutics. Highlights patient-centered care approaches.
Epidemiology and Disease Control
Explores global data trends, incidence patterns, and the burden of rare diseases. Highlights surveillance frameworks, registries, and public health strategies. Focus on identifying unmet needs and improving global disease monitoring.
Biomarker Importance in Rare Diseases
Focuses on the development and validation of biomarkers for diagnosis, prognosis, and therapeutic monitoring. Highlights biomarker-driven trials and precision medicine approaches. Emphasizes early detection and tailored interventions.
Orphan Drug Pricing and Market Dynamics
Explores pricing strategies, reimbursement challenges, and economic models for orphan therapies. Discusses sustainability of innovation, market access barriers, and global disparities in affordability. Highlights patient-centered value assessment frameworks.
Functional Genomics & Gene Therapy for Rare Diseases
Covers how functional genomics accelerates rare disease diagnosis and therapeutic discovery. Focuses on gene therapy success stories, vector advancements, and safety considerations. Examines real-world applications transforming patient lives.
Public Health Perspectives in Rare Diseases
Discusses population-based strategies, national action plans, and global rare disease policies. Highlights advocacy, awareness campaigns, and improving care infrastructure. Emphasizes inclusion and equitable access.
Ethical & Regulatory Challenges
Addresses complex ethical issues in rare disease research, including informed consent, data sharing, and trial equity. Covers regulatory complexities such as adaptive pathways and accelerated approval mechanisms. Focus on balancing innovation with patient safety.
Terms & Condition
Acceptance of Terms and Subsequent Amendments
By using our websites, you fully and legally accept our terms and conditions. we reserve the right to modify these Terms at any time without prior notice. The most current version of the Terms will always be accessible via the link at the bottom of the Site. Continued use of the Site following the posting of any changes constitutes your acceptance of the revised Terms. Please review the Terms periodically for any updates or modifications. If you do not agree to the terms, you are not authorized to use the site.
Conference Registration Payment Methods
Different modes of payment:
Online Mode: Payment for registration can be made separately from the respective conference websites. We have two International Payment gateways: Stripe and PayPal. Both accept payments from all types of cards credit/debit, Visa, Mastercard, and Discover credit cards. American Express cards are not accepted for payment. All the cards must have international transaction enabled. For some payments respective may ask for authorization for completion of registration. We accept in all three currencies USD, EUROs & GBP.
Encryption and Security: the online mod of registration is secured and end to end encrypted. We don’t save or share credit card personal information anywhere, ensuring secure transmission of participant data.
Wire Transfer: Wire/bank transfer can be done from any country. We accept in all three currencies USD, EUROs & GBP.
Offline Mode: This mode of payment is only applicable for cash payment at the registration desk to the conference organizers.
Refund Policies
- Cancellations made more than 60 days before the conference start date will receive a full refund, minus a $150/€150/£150 administrative fee.
- Cancellations made between 59 and 45 days prior to the conference start date will receive a 50% refund.
- Cancellations made less than 45 days before the conference start date are non-refundable.
- Refunds will be processed within 30 days of receiving the cancellation notification and request should be in writing to Conference Mail ID & finance@c2pforum.com.
- The processed refund may take up to 9-10 business days to appear in your account or statement.
- E-poster fees are non-refundable.
- Discounted registrations are nonrefundable in cash or credit.
- In case of visa refusal, the refund policies will be as per time policies or can be transferred to any substitute or any other event only once.
Cancellation Policies
- We strictly adhere to our cancellation policies, and cancellations must be made in writing. we reserve the right to change these policies without prior notice.
- The Organizer holds the sole right to cancel or postpone the conference or webinar in the event of natural disasters, calamities, terrorist activities, pandemics, or other unavoidable and unforeseeable circumstances. Attendees will be informed of any such changes by the respective program managers.
- The Organizer will not be responsible for any loss or damage resulting from the substitution, alteration, postponement, or cancellation of an event due to circumstances beyond its control, including but not limited to force majeure, natural disasters, pandemics, sabotage, accidents, trade or industrial disputes, terrorism, or hostilities.
- If the conference or webinar is cancelled or postponed due to circumstances beyond the Organizer's control, registrations will remain valid for future conferences or webinars. The paid registration and accommodation fees will be automatically carried forward to future events. Refund policies will not apply in these cases.
- If a registrant is unable to attend the rescheduled conference or webinar date, they will be eligible to receive a credit for the full amount paid, which can be used to attend any conference within 12 months.
- The Organizer accepts no liability for personal injuries or for loss or damage to delegates' property during or as a result of the conference or webinar.
Accommodation Cancellation Policies
Respective conference hotels confirm hotel reservations from the organizers only after receiving of full payment. Booked accommodations can be cancelled before 45-30 days before the Check in date. It varies from country-to-country hotel policies. Less than 45-30 days of the event, change in the check in-check out date and cancellation will not be allowed and will not be entitled for refund.
Visa Info
- We urge the attendees to apply for visa in the due course of time ASAP. Registration fees does not include the cost of visa.
- C2P Forum will not contact any embassies for the issuance of visa. We can support by providing invitation letter from organization.
- Under C2P Forum cancelation policy, C2P Forum cannot be held responsible for any participants inability to obtain visas and visa issues cannot be regarded.
Insurance and Transportation
Insurance cost is not included in the registration. Registrants are responsible for their parking and transportation. Shuttle facility to and from airport to hotel varies from hotel to hotel. We request you to obtain correct information of the hotel from conference manager or directly from hotel.
Invitation Letters
Invitation letters will be issued only to the paid registered attendees.
Substitutions and Transfers
If the registrants are unable to attend for any valid reason are eligible to substitute to another speaker or delegate at least 30 days before the event, request should be made in writing to info@c2pforum.com.
Only fully paid registration including Accommodations (in case) are eligible for transfer of their registration fee to the conference scheduled for the following year, if it falls within 12 months from the date of the affected/cancelled conference. However, the organizers reserve the right to approve or deny such transfer requests, likely to manage logistical and administrative considerations. Discounted cost paid towards accommodation are not eligible to transfer. The registrations transferred are not eligible for any reimbursement.
Photos and Filming
Filming or recording the conference presentation are not allowed due to privacy concerns from the attendees. Organizer photographer will take the snaps which will be sent to everyone once we get them after editing post 15 days of the event. Participants not interested in filming need to inform in writing to the organizers in prior.
Unsolicited Commercial E-mail (Anti-Spam) Policy
- At C2P Forum, the privacy of internet users is of paramount importance to us and our customers. We are committed to supporting the protection of client and consumer privacy rights as a fundamental aspect of our business.
- Message Recipient Policy: Clients must consent to receive emails, advertisements, or promotions from us before any such communications are sent. Any recipient may request to be removed from our mailing list at any time, and we will promptly honour such requests. Additionally, we will thoroughly investigate any allegations of unsolicited messages.
- Policy Against Unsolicited Email Advertising: We strictly require that all emails from C2p Forum are sent only to clients who have opted to receive them. We prohibit any advertising of our brand and website via unsolicited email messages. Failure to comply with this policy will result in the termination of partnerships and/or affiliate accounts.
- Unsubscribe at Any Time: Each email sent by C2p Forum will include an easy-to-use unsubscribe link, allowing recipients to remove themselves from our mailing list at any time. If you receive a newsletter or email and decide you no longer wish to receive it, simply click the unsubscribe link at the bottom of the email.
Responsibility
Attendees are sole responsible for the content you upload during the submission process. You must obtain necessary permissions from content owners and indemnify C2P for any failures in obtaining such permissions. C2p will not be responsible for ant third-party content or external links on the website. The attendee will be solely responsible for all their belongings at the venue. Whatever be the reason the organizer will not be responsible for any stolen or missing items of attendees.
Authorization
By registering for the conference, you authorize C2P Forum to capture, record, and utilize your name, likeness, image, and comments. This includes the right to publish, reproduce, exhibit, distribute, broadcast, edit, and/or digitize these materials in publications, advertising materials, or any other form, worldwide, without compensation. Please note that photographing and/or videotaping during any session is strictly prohibited. For any queries, please contact us.
Miscellaneous
Heading in the terms and conditions are given for the convenience of readers. It is highly advisable to readd all the terms and conditions before proceeding as it is completer responsibility of the reader only. For any specific queries or clarification, it is advised to contact the conference manager and C2P directly.